Tiny fish helps clinicians avoid multi-million-dollar treatment for babies suspected of having spinal muscular atrophy

The tiny zebrafish is helping researchers rapidly determine whether a newborn's genetic mutation is likely to cause spinal ...
MedPage Today

Race for the Rheum Disease Cure Heats Up

In June, we reported some of the latest findings on chimeric antigen receptor (CAR) T-cell therapy for rheumatologic conditions such as lupus. In this report, we take a look at what may be coming down ...
walb

From Pain to Possibility: Curing Sickle Cell Disease

NASHVILLE, Tenn. - Sickle cell disease is a devastating, inherited blood disorder that affects an estimated eight million people worldwide and roughly 100,000 here in the United States, most of them ...
ABC7

Family of boy with rare disease that has no known cure fights for faster FDA treatment approvals

"Heart disease, and short stature, larger head, curved fingers, and most of the children do not live past their adolescence," said McKay. There is no known cure for Hunter syndrome, and McKay said ...
KPLC

Researchers say there is now a cure for sickle cell disease

NASHVILLE, Tenn. (Ivanhoe Newswire) - Sickle cell disease is a devastating, inherited blood disorder that affects an estimated eight million people worldwide and roughly 100,000 here in the United ...
WISH-TV

Breakthrough therapies offer hope for sickle cell disease cure

INDIANAPOLIS (WISH) — For the first time, scientists say new therapies have the power to cure sickle cell disease. The disease is a devastating, inherited blood disorder that affects an estimated ...
WNEM-TV

From Pain to Possibility: Curing Sickle Cell Disease

Flint major crime unit investigators are releasing new surveillance video in the unsolved murder of a woman attacked on her 50th birthday. Voters in Saginaw County have a new way to cast a ballot ...
Mother Jones

This Brutal Mosquito-Borne Disease May Have a Cure—But There’s a Catch

Get your news from a source that’s not owned and controlled by oligarchs. Sign up for the free Mother Jones Daily. This story was originally published by Vox and is reproduced here as part of the ...
Morningstar

Cure Rare Disease Awarded $7.4 Million CIRM Grant to Advance Gene Therapy for Limb-Girdle Muscular Dystrophy Type 2i/R9

Cure Rare Disease (CRD) announced it has been awarded a $7.4 million grant from the California Institute for Regenerative Medicine (CIRM) to advance the development of a novel gene therapy for ...
Hosted on MSN

From pain to possibility: Curing sickle cell disease

Sickle cell disease causes excruciating pain and damage to the body. But now there are new treatments that can put an end to patients’ suffering Arkansas to become first state to cut ties with PBS: ...